Among those Robert F. Kennedy Jr. recently named to a federal autism committee are people who tout dangerous treatments and ...

AskBio Inc., an RTP-based gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, has received U.S. Food and Drug Administration (FDA) acceptance of its ...

uniQure N.V. QURE on Friday announced updated preliminary safety and exploratory efficacy data from 11 patients in its Phase ...

Administration in the mid-to-high dose cohorts of the gene therapy trial will pause pending further evaluation.

Scientists reverse eye cell aging with ER-100 gene therapy that reprograms retinal neurons to younger states, offering hope ...

FDA orphan designation for zenocutuzumab‑zbco targets NRG1 fusion–positive advanced cholangiocarcinoma, a small molecular subset within an aggressive malignancy with <15% five-year survival. Orphan ...

Plus500 reports a transformative investment landscape with AI, quantum computing, and clean tech showing significant growth, ...

Two dose-limiting toxicities have been recorded in uniQure’s trial evaluating an investigational AAV gene therapy designed to ...

Roivant and its spinout Priovant said this morning that their immune-modifying drug significantly outperformed placebo in clearing lesions caused by a rare skin disease in a small trial.

Uniqure NV (NASDAQ:QURE) stock gained 3.1% in premarket trading Friday following the company’s announcement of promising preliminary data from its Phase I/IIa t ...

Sustained interest in small molecules, bispecific antibodies, and genomics got the ball rolling in the biotech deals arena in ...

Outsourcing is driving biopharma efficiency and scale, including in the drug discovery area and early phase development.